LIMN
发表于 2025-3-25 07:02:02
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宏伟
发表于 2025-3-25 07:45:19
Gene Therapy Approaches to Treat the Neurodegeneration and Visual Failure in Neuronal Ceroid Lipofusren. Symptoms include vision loss, seizures, motor deterioration and cognitive decline ultimately resulting in premature death. Studies in animal models showed that the diseases are amenable to gene supplementation therapies, and over the last decade, major advances have been made in the (pre)clinic
逃避责任
发表于 2025-3-25 14:34:20
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序曲
发表于 2025-3-25 16:54:25
Optimizing Non-viral Gene Therapy Vectors for Delivery to Photoreceptors and Retinal Pigment Epithells of transgenes have not met the requirements for successful clinical applications so far. The biggest advantage of polymer-based nanoparticle vectors is the ease with which they can be modified to increase their ability to penetrate the cell membrane and target specific cells by simply changing th
鸣叫
发表于 2025-3-25 22:22:15
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印第安人
发表于 2025-3-26 03:42:07
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CRUDE
发表于 2025-3-26 07:35:36
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四海为家的人
发表于 2025-3-26 09:35:38
Success of Gene Therapy in Late-Stage Treatmentdvanced disease stage and analyzed the rescue. We showed stable, sustained rescue of photoreceptor structure and function for at least 1 year, demonstrating gene therapy efficacy after onset of degeneration. The results suggest that RP patients are treatable, even when the therapy is administered at late disease stages.
commune
发表于 2025-3-26 15:43:36
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gratify
发表于 2025-3-26 20:28:42
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