枕垫 发表于 2025-3-28 15:41:10
Development of Antisense Oligonucleotide Gapmers for the Treatment of Dyslipidemia and Lipodystrophy diseases, the translation of the genetic mechanisms into a clinical setting has been quite challenging, with a minimum number of effective treatments available. The advancements in antisense therapy have revolutionized the field of neuromuscular disorders as well as lipid-mediated diseases. With th大方不好 发表于 2025-3-28 19:00:15
http://reply.papertrans.cn/39/3808/380708/380708_42.png难解 发表于 2025-3-29 01:23:39
Degradation of Toxic RNA in Myotonic Dystrophy Using Gapmer Antisense Oligonucleotidesf repeat sequences in the . and . genes, respectively. The expansions are highly unstable and biased for further expansion in somatic cells and across generations. Despite the different genes involved, DM1 and DM2 share several clinical features due to having the similar underlying mechanism of repe软弱 发表于 2025-3-29 04:23:19
http://reply.papertrans.cn/39/3808/380708/380708_44.pngtextile 发表于 2025-3-29 09:27:10
http://reply.papertrans.cn/39/3808/380708/380708_45.png即席 发表于 2025-3-29 14:40:13
Calcium-Mediated In Vitro Transfection Technique of Oligonucleotides with Broad Chemical Modificatioing is the lack of appropriate in vitro validation systems that can predict in vivo activity and toxicity. We have devised a transfection method called CEM (Ca.-enrichment method), where the simple enrichment of calcium ion with calcium chloride in culture medium potentiates the activity of variousPatrimony 发表于 2025-3-29 19:27:27
Evaluating the Knockdown Activity of MALAT1 ENA Gapmers In Vitrotherapeutic purposes. For in vitro evaluation of the knockdown activity of gapmer ASOs, we often use lipofection or electroporation to deliver gapmer ASOs into the cells. Here, we describe a method for evaluating the knockdown activity of gapmer ASOs by a cell-free uptake mechanism, termed as gymnos揭穿真相 发表于 2025-3-29 19:53:21
http://reply.papertrans.cn/39/3808/380708/380708_48.pngType-1-Diabetes 发表于 2025-3-30 00:38:00
Development of LNA Gapmer Oligonucleotide-Based Therapy for ALS/FTD Caused by the C9orf72 Repeat Expisease appears to manifest sporadically. The recent discovery of the hexanucleotide repeat expansion in the C9orf72 gene as the causative agent of ALS (C9ALS) gives rise to the opportunity to develop new therapies directed at this mutation, which is responsible for a large proportion of ALS and/or fBUOY 发表于 2025-3-30 06:04:21
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